Team eyes gene therapy for children paralyzed by rare mutations

October 20, 2023

Turning on the gene in mice restores the animals’ motor functions The 50 families stretch from the Netherlands and the United Kingdom to the United States and China. Each family has a child who is paralyzed from a mutation in a single gene named Contactin-Associated Protein 1 (Cntnap1). The children are locked inside their bodies, […]




PhD candidate breaks new ground with aim to improve quality of life for others

October 20, 2023

Afaf Saliba Jaafar knows firsthand the importance of improving the quality of life for those suffering from challenging medical conditions. Her 12-year-old son Brandon Jaafar has severe autism. “The discovery of therapeutics is indeed a lengthy and complex process,” she said. “Families with loved ones suffering from a certain disease often feel a sense of […]